Columns

Recent Posts

• I’m a wife and mom to a special needs child, but what defines me?
• FDA decision on UX111 gene therapy for Sanfilippo expected in September
• Screen time is a lifeline for our daughter with Sanfilippo syndrome
• Physical therapy eases pain, improves life for Sanfilippo kids: Study
• Being a Sanfilippo parent means facing impossible decisions
• UX111 gene therapy shows long-term benefit in Sanfilippo type A: Trial data
• Our respite caregiver provides much-needed help
• Study says U.S. Sanfilippo societal cost will top $2B over 20 years
• Bone marrow transplant helps hand-eye coordination in Sanfilippo child
• The support system that allows my special needs child to thrive