Developing biomarkers may help support accelerated federal approval for treatments in Sanfilippo syndrome and related diseases. That was the…
Articles by Mary Chapman
A primary goal of this year’s World Sanfilippo Awareness Day, observed annually on Nov. 16, is to get people talking…
The National MPS Society will host its Maritime Gala May 13 on the San Francisco Bay in Tiburon,…
From joining the “Hands of Hope” challenge to adding a Facebook profile frame, supporters globally are poised to mark…
In March, after Alina and Jeremy Croke shared a TikTok video that communicated their $1 million goal to help…
The National Organization for Rare Disorders’ (NORD) “Living Rare, Living Stronger Patient and Family Forum” is back in person…
A film crew visited Alina and Jeremy Croke’s Texas home last spring to make a video about their young son,…
When 11-year-old Connor Ridley heard about another boy named Connor who wants to get into a potentially life-changing clinical trial,…
From posting a photo of their child’s hand in theirs, to switching out their Facebook frame, supporters are poised to…
As part of its Innovative Research Grants Initiative, the National MPS Society has awarded $350,000 to support five projects…