Children with Sanfilippo syndrome type A, including those with severe disease, showed stable or continuously increasing cognitive, language, and motor…
Articles by Steve Bryson, PhD
An examination of brain tissue from a mouse model of Sanfilippo syndrome type D revealed several progressive disease-related features,…
Nerve cells in brain tissue from a Sanfilippo syndrome type C mouse model — in early stages of the…
Altered heparan sulfate metabolism, the underlying cause of Sanfilippo syndrome, leads to dopamine-dependent and autistic-like behaviors in mouse models,…
The Cure Sanfilippo Foundation is encouraging the U.S. Food & Drug Administration (FDA) to consider Sanfilippo syndrome as…
Cure Sanfilippo Foundation has granted $380,000 to the New York-based biotechnology company…
An 11-year-old girl with Sanfilippo syndrome type A who received a stem cell transplant as an infant maintained…
Two types of nerve cells, namely neurons and astrocytes, with Sanfilippo syndrome-like characteristics…
Medical records of children with diseases related to the buildup of glycosaminoglycans, including Sanfilippo syndrome, show that…
Seelos Therapeutics announced it will meet with the European Medicines Agency…