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August 4, 2022 News by Marta Figueiredo, PhD

Sanfilippo Type B Progression Has Similar Trajectory to Type A: Study

Most children with Sanfilippo syndrome type B show predictable downward trajectories in cognitive function, behavior, and brain volume that resemble those of children with rapidly progressing type A, according to data from two natural history studies. Also, most reach their lowest cognitive and adaptive behavior scores by age 8…

October 31, 2019 News by Marta Figueiredo, PhD

Allievex to Continue BioMarin’s Clinical Program Testing Tralesinidase Alfa for Sanfilippo Type B

Allievex, a new clinical-stage biotechnology company founded by Pappas Capital, will continue the clinical program of BioMarin Pharmaceutical‘s tralesinidase alfa (formerly known as BMN 250) for the treatment of people with Sanfilippo syndrome type B. Allievex has obtained an exclusive worldwide license for tralesinidase…

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