Recent Posts
- Balancing logic and emotion isn’t easy as a Sanfilippo parent
- Spruce to move tralesinidase alfa into Phase 3 clinical study
- I’m hopeful about the future of Sanfilippo syndrome type B
- HSPC transplant eases disease symptoms in Sanfilippo C mice
- Forever a toddler: Grieving the independent child I’d dreamed of
- Honoring — and missing — my mother 5 years after her passing
- FDA grants priority review to gene therapy for Sanfilippo type A
- My daughter’s diagnosis with Sanfilippo syndrome type B
- My sister with Sanfilippo is stable for now, so I’m taking a break
- Feeling disconnected from my daughter as Sanfilippo progresses