Author Archives: Iqra Mumal, MSc

Implanting Genetically Corrected Stem Cells Partially Restores Enzyme Activity in Sanfilippo Mice, Study Finds

Brain transplantation of genetically corrected stem cells partially restored enzymatic activity in mice with Sanfilippo syndrome, according to UCLA researchers. Their study, “Genetically Corrected iPSC-Derived Neural Stem Cell Grafts Deliver Enzyme Replacement to Affect CNS Disease in Sanfilippo B Mice,” was published in the journal Molecular Therapy Methods…