• How Are Different Types of Sanfilippo Syndrome Inherited?
  • Alexion Charitable Foundation Giving $1.1M to Assist Rare Disease Community During Pandemic
  • Lysogene CEO Karen Aiach, Inspired by Daughter, Determined to Treat Sanfilippo
  • Feeling Guilty About Moving Away as a Sanfilippo Sibling
  • Reproductive Options for Sanfilippo Syndrome Carriers
  • When Pushing Forward Is the Only Direction to Go
  • FDA Puts Hold on LYS-SAF302 Gene Therapy Trial for Sanfilippo Type A
  • Coalition Will Address Racial Disparities in Rare Disease Communities
  • Sanfilippo Syndrome Type A Versus Type B
  • Seelos Seeks Natural History Data, Rare Disease and Orphan Drug Designations for SLS-005
  • Life Never Stops with Sanfilippo Syndrome
  • Genetic Counseling with Sanfilippo Syndrome and Why It’s Important