• Latest NORD Webinar Offers Insights on Starting Nonprofit, Patient Registry
  • Taysha, Invitae Partner to Offer Genetic Testing for Lysosomal Storage Disorders, Epilepsy
  • Cause of Death Unknown in Child Participating in LYS-SAF302 Gene Therapy Trial
  • Subtypes of Sanfilippo Syndrome
  • NORD Hosting ‘RareLaunch’ Workshops to Help Start Rare Disease Non-profits
  • Hearing Loss Common in Young Patients With MPS Disorders, Study Finds
  • Speech Therapy for Sanfilippo Syndrome
  • The Roller Coaster of Parenting a Special Needs Child
  • ‘Save Connor’ Video Raising Funds for First-ever Clinical Trial in Sanfilippo Type C
  • UK Organization ‘Same But Different’ Announces ‘Glimmer of Hope’ Photo Contest Winner
  • Emotions You May Feel After a Diagnosis of Sanfilippo Syndrome
  • Living My Own Life as a Sanfilippo Sibling