• Grieving My Living Daughter
  • SOBI003 Modified Version of Sulfamidase for Sanfilippo Type A Better at Reaching, Persisting in Brain, Rat Study Suggests
  • Two New NAGLU-deficient Stem Cell Lines May Help Study Sanfilippo Type B
  • How Will Sanfilippo Syndrome Affect My Child’s Life Expectancy?
  • With the New Year Comes Difficult Feelings
  • Lysogene’s Gene Therapy Seen to Correct Enzyme Deficiency in Sanfilippo Type A Mouse Model
  • I’m Struggling with Bitterness This Holiday Season
  • Heparan Sulfate Accumulation May Alter Sulfur Metabolism in Sanfilippo Type B, Mouse Study Suggests
  • Dealing with Jealousy and Other Emotions
  • Gene Therapy Has Potential to Treat Underlying Cause of Sanfilippo, Review Study Finds
  • Gene Therapy Takes Center Stage at 2019 NORD Summit
  • Dealing with the Emotional Toll of Sanfilippo Syndrome