• The COVID-19 Pandemic Shows How the Medically Fragile Often Live
  • NORD Partners with ‘Sing Me a Story’ for July 18–20 Living Rare Forum
  • Global Rare Disease Group’s Focus: 1,000 New Therapies by 2027, Despite COVID-19
  • Tips for Educators of Children With Sanfilippo Syndrome
  • New Sanfilippo-like Cell Lines Created from Stem Cells, Study Contends
  • Building an Individualized Education Plan (IEP) for Children with Sanfilippo Syndrome
  • Rallying Support to Raise Awareness and Find a Cure for Sanfilippo Syndrome
  • Study Examines Newborn Screening for Lysosomal Storage Diseases in Taiwan
  • Pediatric Rare Disease Therapies Increase, But Most Repurposed, Study Finds
  • Early Spinal Surgery May Lessen Nerve Injury in Sanfilippo Syndrome
  • Video: BioNews’ Social Media Campaign Highlights #WhatMakesMeRare
  • Being a Sanfilippo Sibling Will Make Me a Better Teacher