• Xperiome Platform Aims to Streamline Searches for Rare Diseases, Gain Patient Input
  • SLS-005 Given Orphan Drug Designation for Sanfilippo in EU
  • EveryLife Foundation Launches Scholarship Fund for Rare Disease Community in US
  • EMA Committee Gives Positive Opinion on Orphan Drug Status for SLS-005
  • When Do I Tell New Friends About My Sister’s Diagnosis?
  • Seizures in Sanfilippo Syndrome
  • New Streaming Channel Showcases Rare Disease Films
  • How Can Physiotherapy Help My Child With Sanfilippo Syndrome?
  • Stem Cell Therapy May Ease Neurological Symptoms of Sanfilippo Type A, Study Suggests
  • Sanfilippo Syndrome Robs Me of Closure
  • Sanfilippo Syndrome and Sleep
  • Participants Sought for Study to Help Predict Types, Severity of MPS Disorders